Brown University Discovers Cure For Fatal Spinal Muscular Atrophy

May 5, 2017 admin 0

While spinal muscular atrophy (SMA), generally, has still no cure, experts at Brown University have found a “multipronged counterattack” for older patients and their families. […]

New line of attack on spinal muscular atrophy

May 3, 2017 admin 0

Though spinal muscular atrophy (SMA) in its most severe form remains incurable and fatal in early childhood, researchers are sustaining a multipronged counterattack for patients […]

Family raising £10000 to help extend baby Ella’s life

April 27, 2017 admin 0

THE family of a “beautiful and happy” Loughborough baby, battling a rare neuromuscular disorder, are trying to raise £10,000 for treatment that could extend her […]

Nusinersen Improves Motor Function in Children with Spinal Muscular Atrophy

April 26, 2017 admin 0

Data from a phase 3 end of study of nusinersen (Spinraza) demonstrated significant improvement in motor function among children with later-onset spinal muscular atrophy (SMA). […]

Spinal Muscular Atrophy Mouse Models Respond to CK-2127107

March 27, 2017 admin 0

Cytokinetics’ next-generation fast skeletal troponin activator CK-2127107 improves muscle function in mouse models of spinal muscular atrophy (SMA), according to a preclinical trial study. The […]

Children with Spinal Muscular Atrophy Have Poor Bone Health, Study Finds

March 12, 2017 admin 0

Children with spinal muscular atrophy (SMA) have poor bone health that leads to common thigh-bone fractures, regardless of the state of their disease, according to […]

Experimental Spinal Muscular Atrophy Drug Advances Toward FDA Approval

August 18, 2016 admin 0

Nusinersen, an investigational treatment for spinal muscular atrophy (SMA), significantly improved motor milestones and muscle function in babies with infantile onset SMA during a phase […]

Firefighters collecting to give muscular dystrophy the boot

August 6, 2016 admin 0

Gloucester’s firefighters are hitting the streets, not with boots on the ground, but with boots in their hands for a good cause. The city’s firefighters […]